Research News
Research News
Encouraging results from ongoing gene therapy clinical trial...
Abeona Therapeutics presented encouraging results from their ongoing gene therapy clinical trial for...
Monday, 15th Feb 21
Research News
Hopes for a new Sanfilippo type A clinical trial
Researchers at The University of North Carolina have developed a second-generation gene therapy for ...
Monday, 15th Feb 21
Research News
Research spotlight: ERT development for Sanfilippo type D
Towards the end of 2020, American researchers published an enzyme replacement therapy proof-of-conce...
Monday, 1st Feb 21
Fundraising News
Fundraising News
Supporters complete their STEPS FOR SANFILIPPO
89 of our Sanfilippo Supporters set themselves a goal to complete their STEPS FOR SANFILIPPO this No...
Tuesday, 1st Dec 20
Fundraising News
Super sibling Sienna Morrice steps up
Super sibling Sienna Morrice is stepping up this November in honour of her little brother Alec who i...
Wednesday, 25th Nov 20
Fundraising News
Kirkman Kids do Kms for Sanfilippo
Wednesday, 18th Nov 20
Media Highlights
Media Highlights
All for Jane (The Border Mail)
The Border Mail - All for Jane: Jill Kohne is raising awareness of Sanfilippo Syndome, a rare form...
Saturday, 31st Oct 20
Media Highlights
SHEPP LIFE RADIO SHOW & PODCAST: ANN THOMPSON'S SANFILIPPO S...
Ann Thompson shared her Sanfiilppo story in the Backstory segment on the SheppLife Radio Show and Po...
Monday, 12th Oct 20
Fundraising News
How an insidious, untreatable disease broke the heart of a B...
STEPS FOR SKYE bumps Covid-19 off the front page in ‘The Ballarat Courier’. Thank you to this r...
Tuesday, 28th Jul 20
