What is Sanfilippo?
Sanfilippo is a rare genetic condition that causes fatal brain damage. It is a type of childhood dementia and most children never reach adulthood. There is currently no treatment or cure available to children diagnosed with this devastating disease. But there is hope.
With your help we've committed nearly $5.4 million to 33 projects in the search for treatments and a cure for Sanfilippo
Read more about our research strategy and the projects that your generous support makes possible.