What is Sanfilippo?
Sanfilippo is a rare genetic condition that causes fatal brain damage. It is a type of childhood dementia and most children never reach adulthood. There is currently no treatment or cure available to children diagnosed with this devastating disease. But there is hope.
With your help we've directed over $7.5 million to 41 projects in the search for treatments and a cure for Sanfilippo
Read more about our research strategy and the projects that your generous support makes possible.
Research Strategy
Funding Program
Read more about our annual competitive research grant program
Funded Projects
Therapy Avenues
Giving hope to children with Sanfilippo
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Become a regular giver
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Give hope to children with Sanfilippo and their families by including a gift in your will.
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